About 40 million people worldwide are living with HIV infection. In the United Kingdom, there are approximately 100,000 ...

Now Ollie is making history as the world’s first successful gene therapy patient for this cruel condition. Ten months after receiving revolutionary treatment at Royal Manchester Children’s Hospital, ...

As big pharmas including Takeda and Novo Nordisk flee the cell therapy space and smaller biotechs shutter their operations, these players are sticking around to take the modality as far as it can go.

The first child in history has successfully been treated with a new genetic therapy for an ultra-rare developmental defect ...

Oliver Chu is one of five kids participating in a clinical trial investigating a gene therapy for Hunter syndrome, a disorder with symptoms akin to childhood dementia that limits life expectancy ...

Oliver Chu was born with a rare genetic condition called Hunter syndrome that impacts physical and mental development. The ...

A patient says he has "lost total faith" in the NHS after taking prescribed medication he did not need for a year – and still ...

Itvisma (onasemnogene abeparvovec-brve) demonstrated improved motor function and stabilization in patients regardless of SMA treatment history in Phase III studiesOne-time dose of Itvisma replaces ...

The emergence of cancer drug resistance remains one of the most pressing problems in cancer care and there is a critical need ...

The regulator has received reports that a group of patients treated with Adzynma had neutralizing antibodies against the ...

Phage therapy is reshaping our understanding of how targeted viruses can reset the gut microbiome, offering a precise, ...