Doctors looking into hormone therapy as a way to ward off dementia in women

Emerging evidence suggests there may be a critical window for estrogen therapy to protect against cognitive decline later in ...
Smithsonian Magazine

This Toddler Was the First Person to Receive a Test Treatment for a Rare Genetic Disorder. Nine Months Later, His Progress Is Inspiring Hope

Oliver Chu is one of five kids participating in a clinical trial investigating a gene therapy for Hunter syndrome, a disorder with symptoms akin to childhood dementia that limits life expectancy ...

Enzyme discovered in cyanobacteria can add phosphate groups to therapeutic peptides

Researchers from CIIMAR and the University of Helsinki have discovered a new biochemical modification in natural ...
Science Daily

Stanford's new cell therapy cures type 1 diabetes in mice

Researchers at Stanford found a way to cure or prevent Type 1 diabetes in mice using a combined blood stem cell and islet ...

'I've lost faith in the NHS after testing error'

A patient says he has "lost total faith" in the NHS after taking prescribed medication he did not need for a year – and still ...
The Malaysian Reserve

Novartis receives FDA approval for Itvisma®, the only gene replacement therapy for children two years and older, teens, and adults with spinal muscular atrophy (SMA)

Itvisma (onasemnogene abeparvovec-brve) demonstrated improved motor function and stabilization in patients regardless of SMA treatment history in Phase ...
University College London (UCL)

Boy given world-first gene therapy made by UCL scientists ‘thriving’

A young boy born with a devastating, rare genetic condition has been given a new lease of life thanks to a team of UCL ...

Novartis receives FDA approval for Itvisma(R), the only gene replacement therapy for children two years and older, teens, and adults with spinal muscular atrophy (SMA)

ITVISMA is a prescription gene therapy used to treat adults and children 2 years of age and older with spinal muscular atrophy (SMA). ITVISMA is given as a one-time intrathecal injection. What is the ...
Interesting Engineering on MSN

3-year-old boy gets world-first gene therapy to treat life-threatening disorder

A three-year-old Oliver (Ollie) Chu has become the world’s first patient to receive a revolutionary stem cell gene therapy for Hunter syndrome.
Samaa TV

World-first gene therapy transforms life of 3-year-old boy

Three-year-old Oliver becomes first Hunter syndrome patient to receive gene therapy, showing remarkable progress a year after treatment.

Boy, 3, receives 'revolutionary' treatment following world-first Manchester research giving hope to others with rare condition

A three year-old boy with a rare life-limiting condition has undergone a groundbreaking new treatment developed in Manchester ...
The University of Manchester

New hope for children with devastating rare genetic disorder, thanks to world-first research in Manchester

The parents of a three-year-old boy born with a devastating, life-limiting genetic condition say they are now excited for his ...