Much of the phenotypic variation that is observed within and between species is the result of differences in gene regulation: specifically when, where and how much the genes are expressed. Given the ...
While the majority of those infected with SARS-CoV-2 experience only mild symptoms, a significant minority progress to severe or critical symptoms with high rates of mortality. Many risk factors ...
The goal of gene therapy for patients with hemophilia A is to safely impart long-term stable factor VIII expression that predictably ameliorates bleeding with the use of the lowest possible vector ...